Craig M McDonald Selected Research

eteplirsen

3/2024	Survival among patients receiving eteplirsen for up to 8 years for the treatment of Duchenne muscular dystrophy and contextualization with natural history controls.
1/2022	Delays in pulmonary decline in eteplirsen-treated patients with Duchenne muscular dystrophy.
1/2022	A Combined Prospective and Retrospective Comparison of Long-Term Functional Outcomes Suggests Delayed Loss of Ambulation and Pulmonary Decline with Long-Term Eteplirsen Treatment.
1/2021	Comparison of Long-term Ambulatory Function in Patients with Duchenne Muscular Dystrophy Treated with Eteplirsen and Matched Natural History Controls.
1/2021	Open-Label Evaluation of Eteplirsen in Patients with Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping: PROMOVI Trial.
1/2019	Eteplirsen Treatment Attenuates Respiratory Decline in Ambulatory and Non-Ambulatory Patients with Duchenne Muscular Dystrophy.

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Craig M McDonald Research Topics

Disease

67	Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker) 05/2024 - 09/2010
13	Disease Progression 08/2023 - 07/2013
6	Neuromuscular Diseases (Neuromuscular Disease) 05/2021 - 08/2012
5	Cardiomyopathies (Cardiomyopathy) 01/2024 - 12/2013
3	Vomiting 04/2024 - 01/2021
3	Insulin Resistance 01/2019 - 01/2007
3	Spinal Cord Injuries (Spinal Cord Injury) 06/2008 - 01/2007
2	Muscular Dystrophies (Muscular Dystrophy) 04/2024 - 01/2007
2	Growth Disorders 03/2024 - 01/2020
2	Weight Gain 01/2022 - 01/2020
2	Scoliosis 01/2022 - 01/2007
2	Headache (Headaches) 01/2021 - 05/2015
2	Injection Site Reaction 08/2018 - 01/2018
2	Mobility Limitation (Difficulty Walking) 08/2012 - 02/2008
2	Pain (Aches) 08/2012 - 02/2008
1	Liver Diseases (Liver Disease) 01/2024
1	Infections 01/2024
1	Hypersensitivity (Allergy) 12/2022
1	Adrenal Insufficiency (Adrenal Gland Hypofunction) 10/2022
1	Respiratory Tract Infections (Respiratory Tract Infection) 01/2022
1	Cataract (Cataracts) 01/2022
1	Cough 01/2022
1	Inborn Genetic Diseases (Disease, Hereditary) 01/2022
1	Inflammation (Inflammations) 01/2021
1	Fibrosis (Cirrhosis) 01/2021
1	Contracture 01/2020
1	Hirsutism 01/2020
1	Rare Diseases (Rare Disease) 10/2019
1	Lung Diseases (Lung Disease) 11/2018
1	Bone Resorption 10/2018
1	Proteinuria 08/2018
1	Dizziness (Lightheadedness) 03/2018
1	Amyotrophic Lateral Sclerosis (Lou Gehrig's Disease) 03/2018
1	Muscle Cramp (Cramp) 03/2018
1	Chronic Progressive External Ophthalmoplegia (Progressive External Ophthalmoplegia) 08/2017
1	Skin Abnormalities 08/2017
1	Muscle Weakness 07/2016
1	Nasopharyngitis 05/2015
1	Hypoventilation 11/2012
1	Obesity 01/2007
1	Muscular Diseases (Myopathy) 01/2007
1	Metabolic Syndrome (Dysmetabolic Syndrome X) 01/2007

Drug/Important Bio-Agent (IBA)

12	DystrophinIBA 04/2024 - 09/2013
11	Adrenal Cortex Hormones (Corticosteroids)IBA 05/2024 - 09/2010
11	Prednisone (Sone)FDA LinkGeneric 03/2024 - 06/2016
9	deflazacortIBA 01/2023 - 06/2016
8	GlucocorticoidsIBA 05/2024 - 07/2013
8	Nonsense Codon (Nonsense Mutation)IBA 08/2023 - 09/2013
7	atalurenIBA 08/2023 - 09/2013
6	eteplirsenIBA 03/2024 - 01/2019
6	VBP15 compoundIBA 03/2024 - 10/2018
5	Biomarkers (Surrogate Marker)IBA 03/2024 - 10/2018
4	idebenoneIBA 01/2020 - 05/2015
3	SteroidsIBA 01/2023 - 05/2018
3	viltolarsenIBA 01/2023 - 01/2020
3	Proteins (Proteins, Gene)FDA Link 01/2023 - 01/2022
3	domagrozumabIBA 08/2022 - 01/2020
3	Prednisolone (Predate)FDA LinkGeneric 01/2022 - 01/2020
3	Adrenergic Receptors (Adrenergic Receptor)IBA 01/2022 - 10/2019
2	PRO051IBA 08/2018 - 01/2018
1	givinostatIBA 04/2024
1	Glucocorticoid Receptors (Glucocorticoid Receptor)IBA 03/2024
1	Troponin IIBA 01/2024
1	VaccinesIBA 01/2024
1	chenodeoxycholate sulfate conjugate (CDCS)IBA 12/2022
1	Hydrocortisone (Cortisol)FDA LinkGeneric 10/2022
1	Adrenocorticotropic Hormone (ACTH)FDA Link 10/2022
1	Indicators and Reagents (Reagents)IBA 01/2022
1	edasalonexentIBA 01/2021
1	FlavonoidsIBA 01/2021
1	Catechin (Z 7300)IBA 01/2021
1	Mexiletine (Mexitil)FDA LinkGeneric 03/2018
1	Antisense OligonucleotidesIBA 01/2018
1	Tadalafil (Cialis)FDA Link 10/2017
1	Laminin (Merosin)IBA 08/2017
1	Protein Isoforms (Isoforms)IBA 08/2017
1	Angiotensin Receptor AntagonistsIBA 12/2013
1	Losartan (Cozaar)FDA LinkGeneric 12/2013
1	Angiotensin-Converting Enzyme Inhibitors (ACE Inhibitors)IBA 12/2013
1	Lisinopril (Prinivil)FDA LinkGeneric 12/2013
1	HDL LipoproteinsIBA 01/2007
1	Glucose (Dextrose)FDA LinkGeneric 01/2007
1	Triglycerides (Triacylglycerol)IBA 01/2007
1	Insulin (Novolin)FDA Link 01/2007

Therapy/Procedure

14	Therapeutics 01/2024 - 01/2007
3	Orthotic Devices (Orthosis) 06/2008 - 01/2007
2	Self-Help Devices (Assistive Technology) 11/2012 - 02/2008
2	Activities of Daily Living (ADL) 08/2012 - 01/2007
1	Cell- and Tissue-Based Therapy (Cell Therapy) 12/2022
1	Intravenous Infusions 12/2022
1	Investigational Therapies (Experimental Therapy) 05/2021
1	Noninvasive Ventilation 11/2012
1	Artificial Respiration (Mechanical Ventilation) 11/2012
1	Contraindications 08/2012
1	Canes (Cane) 02/2008
1	Braces 01/2007